Skip to main navigation
Skip to search
Skip to main content
Sort by
Keyphrases
Myotonic Dystrophy
100%
Muscleblind-like
85%
Small Molecules
46%
CUG Repeats
25%
Normal Function
23%
Binder
21%
CTG Expansion
21%
RNA Sequencing (RNA-seq)
21%
Sequester
12%
Clinical Model
12%
Binding Specificity
10%
Cell Culture Model
10%
Binding Affinity
10%
Medicinal Chemistry Strategies
10%
Dystrophy
10%
Treatment Options
10%
Protein Kinase
10%
Repeat Sequence
10%
Specific Targeting
10%
MBNL Proteins
10%
Good Target
10%
RNA Interaction
10%
3′-untranslated Region (3′-UTR)
10%
Disease Progression
10%
RNA Splicing
10%
Sequestration
10%
Disease Symptoms
10%
Hairpin
10%
Pre-mRNA
10%
Disease Phenotype
10%
Toxic Gain of Function
10%
Genetic Evidence
10%
Neuromuscular Disorders
10%
Splice Variants
10%
Cellular Process
10%
Specific Aims
10%
Repeat RNA
10%
Acridine
7%
X-ray Crystallography
5%
Rational Design
5%
Toxic RNA
5%
Biochemistry, Genetics and Molecular Biology
RNA
100%
Synapsin I
68%
Small Molecule
37%
RNA Sequence
17%
Untranslated Region
8%
Binding Affinity
8%
RNA Splicing
8%
Protein Kinases
8%
Precursor mRNA
8%
Genetics
8%
Cell Culture
8%
Transcription
8%