A drug candidate for a rare polyalanine disease targeting the protein quality control

  • Sharon Pochtar
  • , Avraham Ashkenazi

Research output: Contribution to journalComment/debate

Original languageEnglish
Article number102364
JournalMolecular Therapy Nucleic Acids
Volume35
Issue number4
DOIs
StatePublished - 10 Dec 2024
Externally publishedYes

ASJC Scopus subject areas

  • Molecular Medicine
  • Drug Discovery

Cite this