Real-Life Outcome After Gene Replacement Therapy for Spinal Muscular Atrophy: A Multicenter Experience

Itay Tokatly Latzer, Liora Sagi, Revital Lavi, Sharon Aharoni, Jacob Bistritzer, Iris Noyman, Mira Ginsburg, Angela Lev-Or, Sharona Katzenellenbogen, Yoram Nevo, Aviva Fattal-Valevski

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Medicine and Dentistry

Pharmacology, Toxicology and Pharmaceutical Science